Steps forward in gene therapy for hearing loss linked to Norrie disease

NDF are excited to share the newly published research paper 'Systemic gene therapy paper rescues retinal dysfunction and hearing loss in a model of Norrie disease'. This paper shares the findings of an international team led by researchers at GOSH, UCL and the National Institute of Health and Care Research Great Ormond Street Hospital Biomedical Research Centre (NIHR GOSH BRC) led by Professor Jane Sowden funded in partnership by GOSHCC & Sparks and the Norrie Disease Foundation https://www.gosh.nhs.uk/news/steps-forward-in-gene-therapy-for-hearing-loss-linked-to-rare-disease/#:~:text=29%20Aug%202023%2C%203%20p.m